The first gene therapy for blindness was used to treat [1],w…
The first gene therapy for blindness was used to treat ,which is caused by a mutation in the gene. This gene normally encodes for a protein necessary for . This is an example of gene therapy, because it is injected directly into the eye. The eye is a good target for gene therapy because they are , and experiments can be performed within the same patient. This is also an example gene therapy. The name of this FDA-approved gene therapy is , and costs per eye.